SAVANNAH, Georgia — There’s no medical treatment for Charcot-Marie-Tooth (CMT) disease ... Most patients with CMT in the United States have type 1A, which is linked to duplication of the ...
Taken together, these data show that onapristone improves the CMT phenotype in Pmp22-transgenic rats by slowing disease progression ... rats than in wild-type rats. (c) Left, transgenic animals ...