Mitochondria In Motion Inc. has identified new N-(trans-4-hydroxycyclohexyl)-6-phenylhexanamide derivatives acting as mitofusin activators and reported to be useful for the treatment of Alzheimer’s, ...
The SynGAP Research Fund 501(c)(3) has awarded a pair of grants to Dr. Clement Chow, a geneticist and Associate Professor in the Department of Human Genetics at the University of Utah. These grants ...
SAVANNAH, Georgia — There’s no medical treatment for Charcot-Marie-Tooth (CMT) disease, a debilitating neurologic disorder that’s both progressive and incurable. But now, nerve specialists ...
In 2021, he revealed that he has Charcot-Marie-Tooth disease. Jackson’s many hits have included “Chasin’ That Neon Rainbow,” “Don’t Rock the Jukebox,” “Little Bitty,” “Remember ...
NMD670 is furthermore being evaluated in two separate Phase 2 trials in patients living with spinal muscular atrophy and Charcot-Marie Tooth Diseases. The gMG Phase2b study, which initiated in June ...
What is sickle cell disease? Sickle cell disease (SCD) is an inherited blood disorder. That means it is passed down from a parent’s genes. It causes the body to make abnormal hemoglobin. Hemoglobin is ...