The FDA approved olezarsen (Tryngolza) as the first drug for adults with familial chylomicronemia syndrome, a rare genetic ...
Affected populations: The disease affects an estimated 1 to 2 people per million every year, according to the National ...
Electricity retailer Geneco has launched a campaign this Chinese New Year to celebrate the strength and spirit of families ...
Familial Alzheimer’s disease is a rare, inherited form of Alzheimer’s that usually develops earlier than other forms of the disease. It’s due to specific genetic variants that tend to run in ...
Early onset familial Alzheimer disease (eFAD) is hereditary and marked by Alzheimer disease symptoms that appear at an unusually early age. Symptoms can start in a person's thirties, forties, and ...
Dilated cardiomyopathy (DCM) is a heterogeneous disorder that is familial in approximately 30% of cases. Although several genes have been identified that can cause familial DCM, molecular analyses ...
ALM-412 is under clinical development by Almirall and currently in Phase I for Familial Adenomatous Polyposis.