The New York Heart Association class improved or remained stable for 77.6% of patients treated with tafamidis as part of an early access program.

Philadelphia chromosome positive ALL had superior outcomes following hematopoietic cell transplantation in first complete remission. Hematopoietic cell transplantation, combined with effective ...

Anxiety reduction was greater with sebetralstat than placebo at both 4 and 12 hours. Results from the phase 3 KONFIDENT clinical trial indicate that sebetralstat, an oral plasma kallikrein inhibitor, ...

Being a primary biliary cholangitis (PBC) advocate is a hard job. It comes with a lot of interpersonal battles as well as challenges I never expected to encounter. Although my advocacy journey feels ...

Which of the statements below about the therapeutic study on Centella asiatica in transthyretin amyloid polyneuropathy (ATTR-PN) are correct? Select one of the options for each question, then submit ...

During treatment with nusinersen there was a mean reduction in performance fatigability of 5.6%. Performance fatigability is an independent component of motor impairment and, therefore, a potential ...

The toxic effect of the TTR amyloid aggregates was reduced in a dose-dependent manner with C. asiatica extract treatment. To explore whether the hydrophilic extract of C. asiatica could suppress the ...

Brain volume loss is not yet a core outcome in relapsing MS clinical trials. However, it is gaining attention due to its correlation with disability progression. Recent findings highlight the value of ...

An analysis examined 9901 online discussions about the MG diagnosis journey in the US. Rates of depressive feelings rose from 14% in the prediagnosis stage to 55% in the ongoing assessment stage.

The substantial growth in myasthenia gravis incidence and prevalence over time could stem, in part, from improved survival, researchers said. SAVANNAH, Georgia—Regional differences aside, studies from ...

Worsening symptoms in generalized MG can manifest as exacerbations and life-threatening crises. Myasthenia gravis onset after age 50 was significantly linked with exacerbation events in patients with ...

(Getty Images) Researchers compared patients who switched to efgartigimod with others who remained on conventional therapies. Patients taking efgartigimod, compared with those on IVIg, had ...